Dr Michelle Teng is trying to develop the world's first treatment for TUBB4a leukodystrophy before it is too late for her 12-year-old daughter Sofia.

The life-threatening genetic condition affects the central nervous system and can lead to an inability to walk, talk and even swallow. Most young patients die before they reach adulthood.

In the UK, it is thought to affect between 60-90 newborns every year.

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